Ataluren
PRECLINICAL
PHASE 1
PHASE 2
PHASE 3
PRE
P1
P2
P3
Edit
Updated: 08/27/2019
Pipeline Type
New Drugs in Development
Phase Of Development
Phase 2
Sponsors and Collaborators
New York University, PTC Therapeutics, Epilepsy Foundation (EF)
Mechanism of Action
RNA Therapy
Mechanism Description
Reads through nonsense mutations
Populations Tested In
Dravet Syndrome
Other Resources
Special FDA Designation
Nonprofit or Government Support
Nonprofit
Nonprofit or Government Support Description
Epilepsy Foundation - NTCG 2016
Previous Presentations
Presented at meetings (latest date) (Pipeline, AEDD; AES, Eilat, etc)
N/A
Location of Clinical Trials
New York, New York
Clinical Trial link